Gene Therapy for Hemophilia
Gene therapy has remained a constant prospect in the sphere of hemophilia treatment. For over two decades and the question remained: Is this just a dream, or could it one day become a reality?Hemophilia gene therapy has finally been approved. David Page talks to hemophilia specialists that will dive deep into understanding how the treatment works, its significance in advancing treatment, and how a one time treatment could change a severe condition to a milder one.Though not a definitive cure, gene therapy for hemophilia has transformed the dream of a cure into a reality for the future.David and his guests will provide exclusive insights into one of the most significant medical breakthroughs of our era.
Recent Episodes
All About Von Willebrand Disease: Von Willebrand Disease 101
2026 marks the 100th year anniversary of when Dr Eric Von Willebrand first described the condition in a five year old girl. With this anniversary, we at the Canadian Hemophilia Society feel it's the perfect time to focus on i...
Shared Decision-Making
Over the last several years, gene therapy for hemophilia B has become a reality. Some received it through clinical trials, and others received it after marketing authorizations and reimbursement approvals in their countries. ...
Four People Describe Their Experiences with Hemophilia B Gene Therapy
Over the last several years, gene therapy for hemophilia B has become a reality. Some received it through clinical trials. Others received it after marketing authorizations and reimbursement approvals in their countries. In t...
If Gene Therapy for Hemophilia B Were Available Tomorrow, Would You W…
For the last 40 years, we have witnessed tremendous advances in care and treatment for people with hemophilia. Gene therapy has been a dream for most of those 40 years, and the last two to three years, two gene therapies for ...
Overview of Gene Therapy Approaches
In this first episode of our second podcast series, GENE THERAPY FOR HEMOPHILIA – FROM DREAM TO REALITY, Dr. David Lillicrap describes what gene therapy is in 2026 and hopefully how it works. Dr. Lillicrap is a Professor in t...
![WEBINAR 2: [FR] Un Pas en Arrière, Deux Pas en Avant](https://content.production.cdn.art19.com/images/6f/d8/7e/9e/6fd87e9e-d7db-4289-8db0-a96060ffe412/b4c917c5b2a0c246e3bcec63fe1e89061ab89086fe25f05424752836aab52c2374e532c2fac0bf9e08eea9a209c8036465fd4ab7468feb05e032521c6949b759.jpeg "WEBINAR 2: [FR] Un Pas en Arrière, Deux Pas en Avant")
WEBINAR 2: [FR] Un Pas en Arrière, Deux Pas en Avant
Le webinaire de la Société canadienne de l'hémophilie a abordé la thérapie génique pour les hémophiles. Dr. Jean St. Louis a expliqué les différences entre les injections de facteurs et la thérapie génique, en utilisant des vecteurs AAV pour introduire des gènes dans les cellules du foie. Il a déta…
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